OLAPARIB-IDH-SARC

NCT03212274 📎

Regimen

Experimental
Olaparib 300 mg PO BID continuous (PARP inhibitor)
Control
none (single-arm)

Population

Advanced IDH1- or IDH2-mutant mesenchymal sarcomas (chondrosarcoma dominant, plus cholangiocarcinoma excluded per design), refractory to standard therapy

Key finding

PARP inhibition in IDH-mutant chondrosarcoma produced durable disease stabilization in the majority of patients, establishing a second biomarker-driven strategy after IDH1 inhibition. Small N but mechanistically coherent.

Source: PMID 34994649

Timeline